Enzyme replacement therapy for alpha-mannosidosis: 12 months follow-up of a single centre, randomised, multiple dose study

Research output: Contribution to journalJournal articleResearchpeer-review

  • Line Gutte Borgwardt
  • Christine I. Dali
  • J Fogh
  • Joan Månsson
  • K J Olsen
  • Hans Christian Beck
  • L H Nielsen
  • S O E Olsen
  • H M F Riise Stensland
  • O Nilssen
  • F Wibrand
  • Anne-Marie Thuesen
  • T Pearl
  • U Haugsted
  • P Saftig
  • J Blanz
  • Sheila Jones
  • A Tylki-Szymanska
  • N Guffon-Fouiloux
  • Marie Valentin Beck
  • A M Lund
Original languageEnglish
JournalJournal of Inherited Metabolic Disease
Volume36
Issue number6
Pages (from-to)1015-1024
Number of pages10
ISSN0141-8955
DOIs
Publication statusPublished - 2013

ID: 118757004