NEO1/NEO-EXT studies: Safety and exploratory efficacy of repeat avalglucosidase alfa dosing after up to 6 years in late-onset Pompe disease (LOPD)

Research output: Contribution to journal › Conference abstract in journal › Research › peer-review

  • B. Schoser
  • R. Barohn
  • B. Byrne
  • O. Goker-Alpan
  • P. Kishnani
  • S. Ladha
  • P. Laforet
  • E. Mengel
  • L. Pena
  • S. Sacconi
  • V. Straub
  • J. Trivedi
  • P. Van Damme
  • A. van der Ploeg
  • Vissing, John
  • P. Young
  • K. Haack
  • I. Ivanina
  • Y. Wang
  • M. Dimachkie
Original languageEnglish
JournalNeuromuscular Disorders
Volume30
Pages (from-to)S49
Number of pages1
ISSN0960-8966
DOIs
Publication statusPublished - Oct 2020
Event25th International Congress of the World-Muscle-Society (WMS) -
Duration: 28 Sep 2020 → 2 Oct 2020

Conference

Conference25th International Congress of the World-Muscle-Society (WMS)
Period28/09/2020 → 02/10/2020

ID: 269512652